![A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access](/proxy.php?image=https%3A%2F%2Fc.biztoc.com%2Fp%2F74858d36b8eb2807%2Fo.webp&hash=19cabae50e63938e4b41c30025635c69)
A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the world’s most expensive medicine. Lenmeldy was approved by the US Food and Drug Administration on Monday and is…
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